Status | Study |
RECRUITING |
Study Name: A Study to Assess Vamorolone in Boys Ages 2 to <4 Years and 7 to <18 Years With Duchenne Muscular Dystrophy (DMD) Condition: Duchenne Muscular Dystrophy Date: 2021-11-09 Interventions: Oral administration of vamorolone for 12 weeks. |
Enrolling by invitation |
Study Name: Long-term Extension Study to Assess Vamorolone in Boys With Duchenne Muscular Dystrophy (DMD) Condition: Duchenne Muscular Dystrophy Date: 2017-01-30 Interventions: Drug: Vamorolone 0.25 mg/day/day |
Not yet recruiting |
Study Name: Clinical Trial to Evaluate the Efficacy, Safety, and Tolerability of BMS-986089 in Ambulatory Boys With Duchenne Muscular Dystrophy Condition: Duchenne Muscular Dystrophy Date: 2017-01-27 Interventions: Biological: BMS-986089 Take BM |
Recruiting |
Study Name: Plus Epicatechin Duchenne Muscular Dystrophy in Non-ambulatory Adolescents Condition: Duchenne Muscular Dystrophy Date: 2016-11-07 Interventions: Drug: (+)- Epicatechin |
Recruiting |
Study Name: An Open-label Extension Study To Evaluate Safety Of PF-06252616 In Boys With Duchenne Muscular Dystrophy Condition: Duchenne Muscular Dystrophy Date: 2016-09-14 Interventions: Biological: PF-06252616 Either 5mg/kg, 20mg/kg or 40mg/kg will be assigned to a subject based on their m |
Completed |
Study Name: Analysis of a Virtual Reality Task in Patients With Duchenne Muscular Dystrophy Condition: Duchenne Muscular Dystrophy Date: 2016-08-17 Interventions: Device: Acquisition on TouchScreen |
Recruiting |
Study Name: An Extension Study to Assess Vamorolone in Boys With Duchenne Muscular Dystrophy (DMD) Condition: Duchenne Muscular Dystrophy Date: 2016-04-28 Interventions: Drug: Vamorolone 0.25 mg/day/day |
Recruiting |
Study Name: A Study to Assess Vamorolone in Boys With Duchenne Muscular Dystrophy (DMD) Condition: Duchenne Muscular Dystrophy Date: 2016-04-28 Interventions: Drug: Vamorolone 0.25 mg/kg/day |
Recruiting |
Study Name: Study of DS-5141b in Patients With Duchenne Muscular Dystrophy Condition: Duchenne Muscular Dystrophy Date: 2016-01-26 Interventions: Drug: DS-5141b DS-5141b, Subcutaneous injection |
Withdrawn |
Study Name: Gene Transfer Clinical Trial for Duchenne Muscular Dystrophy Using rAAVrh74.MCK.GALGT2 Condition: Duchenne Muscular Dystrophy Date: 2015-12-23 Interventions: Biological: rAAVrh74.MCK.GALGT2 |